Tezacaftor

CFTR corrector

Phase of research

FDA-/EMA-approved for Cystic Fibrosis

How it helps

Restore CFTR Function

General information

N/A

Synonyms

VX-661

Marketed as

Dietary sources

N/A

Structure not available

C26H27F3N2O6

Drug-Mutation Relation

results for 2184delA / S1455X
See all data on Tezacaftor

Treats

Mutation Link Tested on Impact factor Notes
S1455X Capitalizing on the heterogeneous effects of CFTR nonsense and frameshift variants to inform therapeutic strategy for cystic fibrosis human cell cultures 5.22 In combination with lumacaftor.

Does not treat

Mutation Link Tested on Impact factor Notes