Bypassing CFTR: An Alternative Approach to Treating Cystic FibrosisIvana Mišová, PhD.
When there is no CFTR protein to be rescued by modulators, we must look elsewhere. Substituting the function of CFTR by another protein could be the answer.
Genetic Therapy of Cystic Fibrosis: The Treatment of TomorrowIvana Mišová, PhD.
Genetic therapy has the potential to revolutionize the world of cystic fibrosis, however, there are still many obstacles to overcome.