Filter the drugs by the phase of research, how they help and the responsive mutations.
Cystic fibrosis is a genetic disease caused by mutations in the CFTR gene. Browse the
database of
drugs treating specific mutations compiled by the AIM tool.
| Drug | Marketed as | Description | Phase of research | How it helps |
|---|---|---|---|---|
| CF(cor)-325 | CFTR corrector |
Pre-clinical | Restore CFTR Function | |
| CFFT-002 | CFTR corrector |
Pre-clinical | Restore CFTR Function | |
| CFFT-003 | CFTR corrector |
Pre-clinical | Restore CFTR Function | |
| CP7q | CFTR potentiator |
Pre-clinical | Restore CFTR Function | |
| CTP-656 | Deuterated Ivacaftor analog, CFTR potentiator |
Phase Two Clinical Trial | Restore CFTR Function | |
| Capsaicin | QUTENZA® | CFTR potentiator |
Accessible Dietary Supplement | Restore CFTR Function |
| Caveolin 2 | CFTR corrector |
Pre-clinical | Restore CFTR Function | |
| Cholera toxin | Rescues endogenous misfolded proteins |
Pre-clinical | Restore CFTR Function | |
| Ciclopirox | CFTR corrector |
FDA-approved for Other Purpose | Restore CFTR Function | |
| Corr-4a | CFTR corrector |
Pre-clinical | Restore CFTR Function |
