Filter the drugs by the phase of research, how they help and the responsive mutations.
Cystic fibrosis is a genetic disease caused by mutations in the CFTR gene. Browse the database of drugs treating specific mutations compiled by the AIM tool.
|Drug||Marketed as||Description||Phase of research||How it helps|
|Tezacaftor||Symdeko® (ivacaftor/tezacaftor), Symkevi® (ivacaftor/tezacaftor), Trikafta™(elexacaftor/tezacaftor/ivacaftor)||
|FDA-/EMA-approved for Cystic Fibrosis||Restore CFTR Function|
Aminoglycoside antibiotic capable of translational readthrough
|FDA-/EMA-approved for Cystic Fibrosis||Anti-Infective,Restore CFTR Function|
|FDA-/EMA-approved for Other Purpose||Restore CFTR Function|