Filter the drugs by the phase of research, how they help and the responsive mutations.
Cystic fibrosis is a genetic disease caused by mutations in the CFTR gene. Browse the
database of
drugs treating specific mutations compiled by the AIM tool.
| Drug | Marketed as | Description | Phase of research | How it helps |
|---|---|---|---|---|
| CF(cor)-325 | CFTR corrector |
Pre-clinical | Restore CFTR Function | |
| CFFT-002 | CFTR corrector |
Pre-clinical | Restore CFTR Function | |
| CFFT-003 | CFTR corrector |
Pre-clinical | Restore CFTR Function | |
| CP7q | CFTR potentiator |
Pre-clinical | Restore CFTR Function | |
| CTP-656 | Deuterated Ivacaftor analog, CFTR potentiator |
Phase Two Clinical Trial | Restore CFTR Function | |
| Caveolin 2 | CFTR corrector |
Pre-clinical | Restore CFTR Function | |
| Cholera toxin | Rescues endogenous misfolded proteins |
Pre-clinical | Restore CFTR Function | |
| Corr-4a | CFTR corrector |
Pre-clinical | Restore CFTR Function | |
| DMA | CFTR corrector and potentiator |
Pre-clinical | Restore CFTR Function | |
| ETX001 | TMEM16A potentiator |
Pre-clinical | Mucociliary Clearance |
