Filter the drugs by the phase of research, how they help and the responsive mutations.

Cystic fibrosis is a genetic disease caused by mutations in the CFTR gene. Browse the database of drugs treating specific mutations compiled by the AIM tool.
Drug Marketed as Description Phase of research How it helps
CF(cor)-325

CFTR corrector

Pre-clinical Restore CFTR Function
CFFT-002

CFTR corrector

Pre-clinical Restore CFTR Function
CFFT-003

CFTR corrector

Pre-clinical Restore CFTR Function
CP7q

CFTR potentiator

Pre-clinical Restore CFTR Function
CTP-656

Deuterated Ivacaftor analog, CFTR potentiator

Phase Two Clinical Trial Restore CFTR Function
Capsaicin QUTENZA®

CFTR potentiator

Accessible Dietary Supplement Restore CFTR Function
Caveolin 2

CFTR corrector

Pre-clinical Restore CFTR Function
Cholera toxin

Rescues endogenous misfolded proteins

Pre-clinical Restore CFTR Function
Ciclopirox

CFTR corrector

FDA-approved for Other Purpose Restore CFTR Function
Corr-4a

CFTR corrector

Pre-clinical Restore CFTR Function